Sarepta Therapeutics Inc

Sarepta Therapeutics Inc is a leading biopharmaceutical company that specializes in developing innovative RNA-targeted therapeutics for rare neuromuscular diseases. The company's mission is to enhance the quality of life for patients with these debilitating conditions by providing effective and safe treatments that address the underlying genetic causes of their diseases. Sarepta's pipeline comprises several promising drug candidates, including exon-skipping therapies for Duchenne muscular dystrophy and gene therapies for limb-girdle muscular dystrophy and Pompe disease. The company is committed to advancing the science of RNA-targeted therapeutics and collaborating with patients, families, and healthcare providers to bring new treatments to market as quickly as possible. With a dedicated team of scientists, researchers, and industry experts, Sarepta is poised to make a significant impact on the lives of patients with rare neuromuscular diseases worldwide.